We are advancing our mRNA pipelines for the treatment of multiple conditions while working to discover new modalities and programs.
| Modality | Candidate | Gene Targets | Indications | Discovery | Proof-of-Concept | Pre-Clinical | IND | Clinical Trial |
|---|---|---|---|---|---|---|---|---|
| mRNA Therapeutics |
PT101 | VEGFA | Heart Failure and Vascular-Related Diseases |
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| PT102 | Ras | Solid Tumors |
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| PT103 | Undisclosed | Blood Cancers |
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| PT104 | Undisclosed | Solid Tumors |
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| mRNA-Engineered Cell Therapies |
PT201 | CD19 | Blood Cancers & Autoimmune Diseases |
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