We are advancing our mRNA pipeline for the treatment of multiple conditions while working to discover new modalities and programs.
mRNA Therapeutics
Program
Target
Indication
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial
PT101
VEGFA
Heart Failure & Vascular-Related Diseases
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial
PT102
Ras
Solid Tumors
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial
PT103
Undisclosed
Hematological Malignancies
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial
PT104
Undisclosed
Solid Tumors
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial
mRNA-Engineered Cell Therapies
Program
Target
Indication
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial
PT201
CD19
Hematological Malignancies & Autoimmune Diseases
Discovery
Proof-of-Concept
Pre-Clinical
IND
Clinical Trial